News
Milestones hit in MD trial testing treatment to turn off faulty gene
10+ hour, 10+ min ago (557+ words) Early data showing evidence of safety, effectiveness of targeted gene therapy Written by Marisa Wexler, MS | July 9, 2026 Two major steps are now complete in an early clinical trial testing a one-time epigenetic therapy " a treatment designed to turn on or…...
GEMMABio Awarded ARPA-H Funding To Pursue Innovative Base-Editing Strategy For Rare Liver Diseases
5+ hour, 6+ min ago (35+ words) Trading View GEMMABio Awarded ARPA-H Funding To Pursue Innovative Base-Editing Strategy For Rare Liver Diseases More news from Reuters...
ARPA-H bookmarks $160 M for custom gene editing treatments. Is it enough?
3+ hour, 10+ min ago (62+ words) Endpoints News ARPA-H book'marks $160 M for cus'tom gene edit'ing treat'ments. Is it enough? Af'ter an in'fant last year was saved from a dead'ly dis'ease thanks to a be'spoke gene edit'ing ther'a'py that fixed an in'cred'i'bly " Think we're worth reading - tell…...
HIV vaccine candidates reach milestone in primates
6+ hour, 5+ min ago (628+ words) Multistep vaccination strategy coaches B cells to raise broadly neutralizing antibodies Since the height of the AIDS crisis, when researchers first began to test possible vaccines against HIV, medical advances have revolutionized living with the virus. But while drugs to…...
Genome editing in rats enables more accurate ER+ breast cancer models
6+ hour, 35+ min ago (463+ words) Rat disease models have played an integral role in scientific discovery and cancer research, including Nobel Prize-winning work from Charles Huggins on hormone therapy for prostate cancer in 1966. However, technical challenges in genetic engineering of rat models have limited their…...
ARPA-H launches $160 million effort to develop custom gene editing drugs
7+ hour, 28+ min ago (206+ words) ARPA-H, the U. S." "moonshot" agency for health research, announced Thursday that it will spend up to $160 million to push forward custom gene editing treatments for a spate of rare diseases." The program, called THRIVE, will back seven different teams pursuing various…...
CRISPR Advances Transform Cancer Diagnosis and Treatment in Clinical
3+ hour, 33+ min ago (150+ words) Oncology Bioengineer. org CRISPR Technologies Propel Cancer Care into a New Era of Precision Medicine Regulatory frameworks also lag behind scientific innovation, necessitating the establishment of clear guidelines for CRISPR-based diagnostics and therapies. Balancing rapid clinical adoption with comprehensive safety…...
Confluence Genetics Launches Cas-CLEAR, a New CRISPR Technology Platform for Cancer Therapy
3+ hour, 43+ min ago (547+ words) Bio Space Confluence Genetics Launches Cas-CLEAR, a New CRISPR Technology Platform for Cancer Therapy Cas12a2-based approach designed to eliminate cancer cells carrying defined genetic signatures while sparing healthy cells Lead programs in development for the treatment of hepatocellular carcinoma, including…...
Scientists Could Use the Brain's Cleanup System To Deliver Gene Therapy
9+ hour, 8+ min ago (524+ words) The platform pairs specially engineered adeno-associated viruses (AAVs) with a delivery strategy that harnesses the brain's natural fluid transport pathways. Together, these innovations enabled researchers to deliver therapeutic genes broadly throughout the brain, preferentially targeting human glial cells while minimizing…...
Astra Zeneca-Ionis drug fails to meet main goal in late-stage heart disease trial
16+ hour, 18+ min ago (61+ words) Yahoo July 9 (Reuters) - Astra Zeneca "said on "Thursday that "its drug Wainua, made "in "partnership with Ionis, "failed to "meet "the main "goal "of reducing cardiovascular deaths and recurring "heart "problems "in "a "late-stage trial. (Reporting by "Raechel "Thankam Job…...